Found 2 clinical trials
Treatment of Refractory Diamond-Blackfan Anemia With Eltrombopag
At 6 months, they will repeat all the screening tests and also have: Quality-of-life questionnaire Neurodevelopmental test (for participants younger than 18 years) If participants blood cell counts improve, they may keep taking eltrombopag for up to 3 more years. If so, they will have blood taken every 4 weeks. …
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- 19 Feb, 2024
A Study of Enasidenib in People With Clonal Cytopenia of Undetermined Significance
Study researchers think that a drug called enasidenib may help people with clonal cytopenia of undetermined significance (CCUS) because the drug blocks the mutated IDH2 protein, which may improve blood cell counts. The purpose of this study is to find out whether enasidenib is a safe and effective treatment for …
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- 02 Dec, 2024